Adeno-associated virus (AAV) vector-based gene therapies have revolutionised medicine, offering life-changing efficacy for various diseases, including AAV2-based Luxturna for previous medically untreatable retinal dystrophy, AAV9-based Zolgensma for spinal muscular atrophy, and AA5-based Hemgenix for hemophilia. Read more
2 May 2025
PhD Research Project
Funded PhD Project (UK Students Only)