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muscular dystrophy PhD Projects, Programs & Scholarships

We have 7 muscular dystrophy PhD Projects, Programs & Scholarships

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We have 7 muscular dystrophy PhD Projects, Programs & Scholarships

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Gene therapy development for various muscular dystrophies

Our research focuses on the pre-clinical development of gene therapies for neuromuscular diseases, in particular the muscular dystrophies based on gene addition, endonuclease-mediated gene editing, antisense oligonucleotide (AO)-induced exon skipping and gene silencing. Read more

CRISPR manipulation of gene expression in retinal organoids to model and rescue human disease

Human pluripotent stem cells can be used in the lab to grow 3D retinal structures called retinal organoids. This allows us to investigate both the early and later events of human eye development and disease. Read more

CRISPR-activation to prevent genetic eye disease

Mutations causing a lack of sufficient protein activity resulting from haploinsufficiency or hypomorphic alleles are the cause of most inherited retinal dystrophies (IRDs). Read more

Development of a personalized therapy for pulmonary arterial hypertension (PAH)

  Research Group: Pharmacology and Experimental Therapeutics
Pulmonary arterial hypertension (PAH) is a devastating cardiovascular disorder which, if left untreated, leads to heart failure and death. Read more
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